#RareAsOne: 7,000 rare diseases, 1 fight

Rare disease patients and their families share their experiences living with a rare disease. Learn about their efforts to drive forward research and find cures.

Emily Kramer-Golinkoff, Dr. David Fajgenbaum, Dr. Maria Kefalas and her daughter Cal, Nasha Fitter and her daughter Amara, Onno Faber, and Tracy Dixon-Salazar and her daughter Savannah all have one thing in common: rare disease. Their journeys may be different, but their fight to find a cure connects them.

“We’re going to have a front row seat to the biggest medical breakthrough in a generation.” – Dr. Maria Kefalas

Meet these fearless rare disease patients and their families and learn more about their efforts to drive forward progress against rare disease.

This video was directed by Joanna Rudnick.

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